%0 Journal Article
%K Animal model flaws
%K Bietti Crystalline Dystrophy
%K Cyp4v3 knockout mouse
%K Genetic background
%K Interspecies differences
%K Orphan Drug Development
%K Patient perspective
%K Rare Disease Research
%K Transparent science
%B Orphanet Journal of Rare Diseases
%D 2023
%N 1
%P 14
%R 10.1186/s13023-022-02557-6
%T A patient advocating for transparent science in rare disease research
%U https://doi.org/10.1186/s13023-022-02557-6
%V 18
%8 2023-01-19